ARTICLE | Politics, Policy & Law
Rare disease crisis requires global approaches
By Steve Usdin, Washington Editor
December 7, 2024 12:01 AM UTC
Terms like “orphan” and “ultrarare” have been effective organizing principles for research and public policy, but they can also obscure the scale and urgency of suffering caused by low-prevalence diseases. As the patient community has documented, while the number of people with each specific rare disease diagnosis is small, tens of millions of people around the world are affected by a rare disease and most have no effective treatments.
Geographic issues that are problematic for all drug development, such as inconsistencies in regulatory requirements, differences in incentives, and barriers to data collection, are especially troublesome for rare diseases. …
- SEO Powered Content & PR Distribution. Get Amplified Today.
- PlatoData.Network Vertical Generative Ai. Empower Yourself. Access Here.
- PlatoAiStream. Web3 Intelligence. Knowledge Amplified. Access Here.
- PlatoESG. Carbon, CleanTech, Energy, Environment, Solar, Waste Management. Access Here.
- PlatoHealth. Biotech and Clinical Trials Intelligence. Access Here.
- Source: https://www.biocentury.com/article/654406/international-regulators-collaborating-on-rare-diseases